A man from Norway has likely been cured of HIV after receiving a stem cell transplant from his brother, who has two copies of ...

As we age, our cells accumulate genetic changes—mutations—some of which open the door to cancer. Scientists call these ...

A 64-year-old Norwegian man appears to have been cured of HIV following a stem cell transplant from his sibling. The patient, ...

In 2025, baby KJ Muldoon became the first person to receive a personalized gene editing treatment, which likely saved his ...

A common genetic mutation linked to alcohol intolerance may also play a far more dangerous role in heart disease than previously understood.

The 64-year-old stopped antiretroviral medication 24 months after a transplant for bone marrow cancer, after his brother was ...

A newly identified gene mutation may help explain why schizophrenia patients struggle to update their understanding of reality. The mutation disrupts a brain circuit involved in flexible ...

Tatiana Schlossberg, the youngest granddaughter of President John F. Kennedy, recently revealed she was diagnosed with terminal acute myeloid leukemia (AML) due to a rare genetic anomaly. In a ...

A surprising discovery from high-altitude animals like yaks and Tibetan antelopes could reshape how we treat nerve damage in humans. Scientists found that a genetic mutation helping these animals ...

Every few months for the past three years, Jeff Vierstra has been receiving infusions in his spine that target and disable a ...

Scientists have corrected an extremely rare and life-threatening genetic disease of the liver in mouse models and human ...